For the first time in Denmark, people with hemophilia B have been treated with the gene therapy Hemgenix (etranacogene ...

Metagenomi says it hopes to start clinical trials next year to test MGX-001, its gene-editing therapy candidate for ...

Columnist Jennifer Lynne, a veteran of Florida hurricanes, offers advice for those with bleeding disorders should evacuations be necessary.

Be Biopharma has raised $92 million to support the first-in-human Phase 1/2 trial of BE-101, which is made to lower bleeding ...

Columnist Joe MacDonald reflects on how the Parents Empowering Parents program helped him and his wife manage their son's hemophilia.

Columnist G Shellye Horowitz explains why she joined a federal lawsuit against a California law requiring licensing for out-of-state doctors.

My husband, Jared, often spent his childhood navigating two very different worlds. In one, he was a regular kid with big dreams and boundless imagination. In the other, he was a young boy living with ...

Now that his adult sons are managing their own hemophilia care, columnist Joe MacDonald is able to consider moving for a job.

I don’t recall when I met Debbie Murray, but I remember the impression she left on me. Her frustration with the long and challenging journey to a proper diagnosis and effective treatment of her ...